12
1300:Biochemistry, Genetics and Molecular Biology(比率: 45.2 %)
| DOI | タイトル | 著者 | ジャーナル | 発行年 | 科研費成果論文 |
|---|---|---|---|---|---|
| 10.1016/j.omtm.2018.06.006 | Prevalence Of Pre-Existing Antibodies To Crispr-Associated Nuclease Cas9 In The Usa Population | Simhadri, Vijaya L.; Mcgill, Joseph; Mcmahon, Shane; Wang, Junxia; Jiang, Haiyan; Sauna, Zuben E. | Molecular Therapy - Methods & Clinical Development | 2018 | NA |
| 10.1016/j.ymthe.2020.04.017 | Aav-Crispr Gene Editing Is Negated By Pre-Existing Immunity To Cas9 | Li, Ang; Tanner, Mark R.; Lee, Ciaran M.; Hurley, Ayrea E.; De Giorgi, Marco; Jarrett, Kelsey E.; Davis, Timothy H.; Doerfler, Alexandria M.; Bao, Gang; Beeton, Christine; Lagor, William R. | Molecular Therapy | 2020 | NA |
| 10.1038/s41467-018-05843-9 | Cas9 Immunity Creates Challenges For Crispr Gene Editing Therapies | Crudele, Julie M.; Chamberlain, Jeffrey S. | Nature Communications | 2018 | NA |
| 10.1038/s41467-019-09693-x | Multifunctional Crispr-Cas9 With Engineered Immunosilenced Human T Cell Epitopes | Ferdosi, Shayesteh R., 0000-0002-2550-8789; Ewaisha, Radwa, 0000-0002-7473-9831; Moghadam, Farzaneh, 0000-0003-3300-4027; Krishna, Sri, 0000-0003-4994-3758; Park, Jin G., 0000-0001-6481-9590; Ebrahimkhani, Mo R., 0000-0001-5753-6779; Kiani, Samira, 0000-0003-2695-1501; Anderson, Karen S. | Nature Communications | 2019 | NA |
| 10.1038/s41467-019-12449-2 | High Levels Of Aav Vector Integration Into Crispr-Induced Dna Breaks | Hanlon, Killian S.; Kleinstiver, Benjamin P., 0000-0002-5469-0655; Garcia, Sara P., 0000-0003-3312-6454; Zaborowski, Miko<U+0142>aj P., 0000-0002-4400-6688; Volak, Adrienn; Spirig, Stefan E.; Muller, Alissa; Sousa, Alexander A.; Tsai, Shengdar Q., 0000-0001-9161-3993; Bengtsson, Niclas E.; Loov, Camilla; Ingelsson, Martin; Chamberlain, Jeffrey S.; Corey, David P.; Aryee, Martin J., 0000-0002-6848-1344; Joung, J. Keith, 0000-0001-5630-5645; Breakefield, Xandra O.; Maguire, Casey A.; Gyorgy, Bence, 0000-0003-0766-6246 | Nature Communications | 2019 | NA |
| 10.1038/s41591-018-0204-6 | High Prevalence Of Streptococcus Pyogenes Cas9-Reactive T Cells Within The Adult Human Population | Wagner, Dimitrios L., 0000-0002-2189-3579; Amini, Leila, 0000-0003-4855-5905; Wendering, Desiree J.; Burkhardt, Lisa-Marie, 0000-0002-9598-2304; Akyuz, Levent; Reinke, Petra; Volk, Hans-Dieter, 0000-0002-7743-6668; Schmueck-Henneresse, Michael | Nature Medicine | 2018 | NA |
| 10.1038/s41591-018-0326-x | Identification Of Preexisting Adaptive Immunity To Cas9 Proteins In Humans | Charlesworth, Carsten T.; Deshpande, Priyanka S.; Dever, Daniel P.; Camarena, Joab; Lemgart, Viktor T.; Cromer, M. Kyle; Vakulskas, Christopher A., 0000-0001-8510-4332; Collingwood, Michael A., 0000-0002-8849-4038; Zhang, Liyang; Bode, Nicole M., 0000-0001-7209-303X; Behlke, Mark A., 0000-0002-4218-857X; Dejene, Beruh; Cieniewicz, Brandon, 0000-0003-3268-7444; Romano, Rosa; Lesch, Benjamin J.; Gomez-Ospina, Natalia, 0000-0002-6740-1154; Mantri, Sruthi; Pavel-Dinu, Mara; Weinberg, Kenneth I.; Porteus, Matthew H., 0000-0002-3850-4648 | Nature Medicine | 2019 | NA |
| 10.1038/s41591-019-0344-3 | Long-Term Evaluation Of Aav-Crispr Genome Editing For Duchenne Muscular Dystrophy | Nelson, Christopher E.; Wu, Yaoying; Gemberling, Matthew P.; Oliver, Matthew L.; Waller, Matthew A.; Bohning, Joel D.; Robinson-Hamm, Jacqueline N.; Bulaklak, Karen; Castellanos Rivera, Ruth M.; Collier, Joel H.; Asokan, Aravind; Gersbach, Charles A., 0000-0003-1478-4013 | Nature Medicine | 2019 | NA |
| 10.1038/s41591-019-0738-2 | Somatic Gene Editing Ameliorates Skeletal And Cardiac Muscle Failure In Pig And Human Models Of Duchenne Muscular Dystrophy | Moretti, A., 0000-0001-5782-7832; Fonteyne, L.; Giesert, F.; Hoppmann, P.; Meier, A. B.; Bozoglu, T.; Baehr, A.; Schneider, C. M.; Sinnecker, D., 0000-0002-8116-9750; Klett, K.; Frohlich, T.; Rahman, F. Abdel; Haufe, T.; Sun, S., 0000-0002-9584-9909; Jurisch, V.; Kessler, B.; Hinkel, R.; Dirschinger, R.; Martens, E.; Jilek, C.; Graf, A., 0000-0003-4435-6861; Krebs, S.; Santamaria, G.; Kurome, M.; Zakhartchenko, V.; Campbell, B.; Voelse, K.; Wolf, A.; Ziegler, T.; Reichert, S.; Lee, S.; Flenkenthaler, F.; Dorn, T.; Jeremias, I., 0000-0003-1773-7677; Blum, H.; Dendorfer, A.; Schnieke, A.; Krause, S.; Walter, M. C.; Klymiuk, N.; Laugwitz, K. L.; Wolf, E.; Wurst, W.; Kupatt, C., 0000-0002-3611-1218 | Nature Medicine | 2020 | NA |
| 10.1126/sciadv.aav4324 | Crispr-Cas9 Corrects Duchenne Muscular Dystrophy Exon 44 Deletion Mutations In Mice And Human Cells | Min, Yi-Li, 0000-0001-6205-9428; Li, Hui, 0000-0002-4114-8349; Rodriguez-Caycedo, Cristina, 0000-0003-3814-2875; Mireault, Alex A., 0000-0002-7534-636X; Huang, Jian; Shelton, John M., 0000-0002-2949-1638; Mcanally, John R., 0000-0001-6938-2703; Amoasii, Leonela; Mammen, Pradeep P. A., 0000-0001-5688-7091; Bassel-Duby, Rhonda, 0000-0001-7568-410X; Olson, Eric N., 0000-0003-1151-8262 | Science Advances | 2019 | NA |
| 10.1126/science.aau1549 | Gene Editing Restores Dystrophin Expression In A Canine Model Of Duchenne Muscular Dystrophy | Amoasii, Leonela, 0000-0001-7960-2749; Hildyard, John C. W., 0000-0003-2283-2118; Li, Hui, 0000-0002-4114-8349; Sanchez-Ortiz, Efrain, 0000-0001-9358-1630; Mireault, Alex, 0000-0002-7534-636X; Caballero, Daniel, 0000-0001-9232-8991; Harron, Rachel, 0000-0001-9418-0708; Stathopoulou, Thaleia-Rengina, 0000-0003-4666-2002; Massey, Claire, 0000-0003-0823-6547; Shelton, John M., 0000-0002-2949-1638; Bassel-Duby, Rhonda, 0000-0001-7568-410X; Piercy, Richard J., 0000-0002-4344-6438; Olson, Eric N., 0000-0003-1151-8262 | Science | 2018 | NA |
| 10.1146/annurev-med-081117-010451 | Crispr Correction Of Duchenne Muscular Dystrophy | Min, Yi-Li; Bassel-Duby, Rhonda; Olson, Eric N. | Annual Review Of Medicine | 2019 | NA |